Baby's Rare Gene-Editing Therapy Offers Hope for Families

A Pennsylvania family's life changed forever when their baby, KJ Muldoon, was diagnosed with CPS1 deficiency, an incredibly rare genetic disorder. The first six months of his life were spent in the hospital. His parents, Kyle and Nicole Muldoon, faced unimaginable challenges. "When the doctor came over and said, 'Your son is very sick,' it was devastating," Nicole recalled. But hope emerged when doctors at Children's Hospital of Philadelphia offered a cutting-edge, personalized gene-editing therapy. KJ became the first patient to undergo this treatment. The procedure was a success, and after 307 days, KJ was finally able to go home. The family's joy was evident in the heartwarming video of KJ's discharge, where the entire hospital staff lined the hallway to cheer him on. While KJ's journey isn't over, his family is grateful for this medical miracle and the promise it holds for other families facing similar challenges.